Tag: Gene therapy
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Hemophilia: Understanding the Disease and Treatment Options
Hemophilia is a rare genetic disorder that affects the ability of the blood to clot properly. People with hemophilia have a deficiency or dysfunction of one of the clotting factors, which can result in excessive bleeding and bruising. In this article, we will discuss the causes, symptoms, and treatment options for hemophilia. What is Hemophilia?…
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Beta Thalassemia: Understanding the Inherited Blood Disorder
Beta thalassemia is a group of inherited blood disorders that affect the production of beta globin, a component of hemoglobin, the protein in red blood cells that carries oxygen to the body’s tissues. When there is a defect in the HBB gene, which produces the beta globin, the body produces abnormal hemoglobin, leading to…
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Understanding Alpha Thalassemia: Symptoms, Diagnosis, and Treatment
Alpha thalassemia is a genetic blood disorder that affects the production of the alpha globin subunit of hemoglobin, a protein in red blood cells that carries oxygen to the body’s tissues. The condition is caused by mutations in the HBA1 and HBA2 genes and it is passed down from parents to their children through…
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Thalassemia: Understanding the Inherited Blood Disorder
Introduction Thalassemia is a group of inherited blood disorders that affect the production of hemoglobin, the protein in red blood cells that carries oxygen to the body’s tissues. The condition is characterized by the abnormal formation of hemoglobin, leading to the destruction of red blood cells and a shortage of oxygen in the body….